GENE therapy may finally be living up to its promise. Injecting “repair genes” into the eyes of six people with a hereditary visual impairment has improved the vision of four of them.
This week, two independent teams announced the results of gene therapy trials in people with Leber congenital amaurosis (LCA), a rare, debilitating disease which causes retinal cells to die off gradually from an early age.
One of the people treated found his sight improved to the point where he could navigate an obstacle course in dim light – a task that had been a struggle before the treatment…
